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CNS Seminar: Ex Vivo Gene Therapy in Leukodystrophies

Join us on Tuesday, February 24, 2026, at 3:00 p.m. CT for an engaging CNS seminar on the rapidly evolving landscape of ex vivo gene therapy for leukodystrophies. This live, virtual program offers 1.25 CME credits and is approved for AMA PRA Category 1 Credit™. The session will be recorded and posted to the CNS Education Center within two weeks (OnDemand available as non-CME).

Hear from leading experts as they explore newly FDA-approved ex vivo gene therapy treatments for X-linked adrenoleukodystrophy and metachromatic leukodystrophy. The seminar will highlight patient eligibility, clinical risks, and prognosis, with a strong focus on the critical role of early diagnosis in achieving optimal outcomes.

Speakers
Amy T. Waldman, MD, MSCE
Laura Ann Adang, MD, PhD, MSTR

Register Here