Join us on Tuesday, March 10, 2026, at 3:00 p.m. CT for an engaging CNS seminar on the rapidly evolving landscape of ex vivo gene therapy for leukodystrophies. This live, virtual program offers 1.25 CME credits and is approved for AMA PRA Category 1 Credit™. The session will be recorded and posted to the CNS Education Center within two weeks (OnDemand available as non-CME).
Hear from leading experts as they explore key factors that contribute to success and the modifiable barriers that contribute to failure is paramount to improving access to urgently needed treatments in the rare disease community. This seminar will highlight recent and current examples of successes and failures of the treatment pipeline for Batten Diseases (Neuronal Ceroid Lipofuscinoses, NCLs), a family of rare neurodegenerative childhood conditions.
Speakers
Jennifer Vermilion, MD, FCNS
Ineka Whiteman, PhD
Yael Shiloh-Malawsky, MD