Please join our expert faculty for an On Demand recording of an educational symposium originally presented at the 50th Child Neurology Society (CNS) Annual Meeting as they:
- Provide an overview of aromatic L-amino acid decarboxylase (AADC) deficiency and the eladocagene exuparvovec construct
- Review clinical experience with treatment options in development for AADC deficiency
- Provide rationale for the putamen as a target delivery site for central nervous system gene therapy
- Discuss the real-world experience of treating patients with investigational eladocagene exuparvovec
Dr. Ashutosh Kumar
Assistant Professor, Pediatrics and Neurology, Penn State Health Milton S. Hershey Medical Center
Dr. Daniel J. Curry
Director, Functional Neurosurgery & Epilepsy Surgery, Texas Children’s Hospital
Prof. Agathe Roubertie
Department of Pediatric Neurology, Hôpital Gui de Chauliac, Montpellier, France
Dr. Matthew Klein
Chair, Chief Development Officer, PTC Therapeutics
ON DEMAND LINK: https://www.ptcbio.com/advancing-the-care-of-a-pediatric-neurotransmitter-disorder/
FINANCIAL SUPPORT BY: PTC Therapeutics